Accomplished RNA therapeutics leader with track record of advancing novel genetic medicines from discovery to FDA approval to ...

Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.

Genetic disorders occur due to alterations in the primary genetic material, deoxyribonucleic acid (DNA), of an organism.

Infection with the pathogenic yeast fungus Candida auris (C. auris) can wreak havoc on the health of hospital patients and ...

Nick Edwards, PhD, CEO of Potato, has a “burning desire” to speed up scientific discovery. In an interview with GEN, he explained how Potato’s AI “scientist,” named Tater, recently replicated a main ...

CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...

In his annual letter, Flagship Pioneering’s Noubar Afeyan lays out a choice between near-term “human-made miracles” and a ...

A large genetic screen has revealed how stem cells transform into brain cells, exposing hundreds of genes that make this ...

Gene-editing technologies show great promise for medical treatments and research, with the potential to cure thousands of ...

The startup aims to create a platform for treating extremely rare genetic mutations, armed with CRISPR advances and new regulatory pathways.

The gene therapy success with Baby KJ, along with a new FDA program, have companies more interested in treating rare disease.

Using its economic leverage, California has been forging its own path on scientific research for 25 years. Here’s how.