The gene therapy success with Baby KJ, along with a new FDA program, have companies more interested in treating rare disease.

The study used large-scale CRISPR gene-editing technology to systematically determine which genes are required as embryonic ...

He Jiankui spent three years in prison after creating gene-edited babies. Now back at work, he sees a greater opening for ...

A large genetic screen has revealed how stem cells transform into brain cells, exposing hundreds of genes that make this ...

In his annual letter, Flagship Pioneering’s Noubar Afeyan lays out a choice between near-term “human-made miracles” and a ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

Converge Bio, the AI platform for accelerated drug discovery and development, announced today $25 million in Series A funding, bringing its total raised to $30 million. The round was led by Bessemer ...

Using its economic leverage, California has been forging its own path on scientific research for 25 years. Here’s how.

Intellia Therapeutics, Inc. (NASDAQ:NTLA), a leading clinical-stage gene editing company focused on revolutionizing medicine ...

A stretch of viral DNA in the mouse genome gives cells in early-stage embryos the potential to become almost any cell type in ...

Shifting regulatory policies and evolving US drug pricing dynamics have created a favourable environment for deals.

But hundreds of thousands of people globally each year won’t survive their bouts with the flu, and millions more will suffer ...