For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...

Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...

A compact Cas12f nuclease shows high editing efficiency in human cells, with structural insights enabling an engineered variant potentially suited for future AAV‑compatible delivery.

Now, following up on that success, a large Chinese collaboration has followed up with a description of an improved gene ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

The last time The Lancet Microbe featured an Editorial on CRISPR was in November 2020, to mark that year’s Nobel Prize in Chemistry, jointly awarded to Emmanuelle Charpentier and Jennifer A Doudna for ...

CRISPR Cas9 genome editing has transformed the way scientists approach gene therapy, acting like precise DNA scissors that can target and repair hereditary diseases at the genetic level. This ...

The ACC has published a scientific statement regarding the use of gene editing therapy for cardiovascular disease.

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using CRISPR-Cas9 in combination with AAV6 vectors can trigger inflammatory and ...

For the first time, a research team at the Leibniz Institute of Plant Genetics and Crop Plant Research (IPK) has succeeded in ...

The US Food and Drug Administration released a draft guidance document on Tuesday with recommendations for using ...